Life Sciences & Biotechnology Companies

Supporting rare disease and oncology development and commercialization with patient-level data and AI-powered Insights

Powering Treatments for Rare Disease & Oncology

From clinical development, to real world evidence, to commercialization, our platform enables breakthrough treatments for diseases of high unmet medical need
We serve established and specialized pharma and biotech firms dedicated to rare diseases, oncology, and niche sub-populations by providing the data and AI tools necessary for:
Clinakos offers the unique ability for organizations to Build Your Own Patient Data Network and Registries, allowing for customized data collection and long-term monitoring of specific niche populations

Key Applications for Pharma & Biotech

Real applications of Clinakos data across the drug development lifecycle.

Pharmaceutical Companies

Accelerate rare disease drug development with real-world patient data that’s nearly impossible to find elsewhere.

Biotech & Startups

De-risk early development with comprehensive patient insights for ultra-rare diseases and novel cancer targets.

Research Use Cases

Real applications of Clinakos data across the rare disease and oncology ecosystem.

Natural History Studies

Understand disease progression, symptom burden, and outcomes for rare diseases with limited published data.

Clinical Trial Design

Inform eligibility criteria, endpoint selection, and sample size calculations with real patient data.

Treatment Patterns

Analyze current standard of care, treatment sequencing, and therapy utilization in rare disease populations.

Comparative Effectiveness

Generate real-world evidence comparing treatment options where randomized trials are not feasible.

Patient Identification

Find eligible patients for clinical trials or expanded access programs based on detailed inclusion criteria.

Health Economics

Conduct cost-effectiveness analysis and budget impact modeling with real utilization data.

Disease Repositories

Patient panels available for 1,500+ rare diseases and oncology indications across therapeutic areas.

Genetic Disorders

Inherited metabolic diseases, lysosomal storage disorders, muscular dystrophies

Rare Cancers

Sarcomas, neuroendocrine tumors, rare hematologic malignancies

Autoimmune

Systemic sclerosis, vasculitis, myositis syndromes

Neurological

ALS, rare epilepsies, neurodegenerative diseases

Hematology

Rare anemias, bleeding disorders, bone marrow failure syndromes

Pulmonary

Pulmonary hypertension, interstitial lung diseases, cystic fibrosis

Endocrine

Rare diabetes types, growth disorders, pituitary diseases

Pediatric

Congenital anomalies, childhood cancers, developmental disorders

Case Study

“Clinakos provided us with curated patient data for a ultra-rare genetic disorder affecting fewer than 500 patients in the US. Their Medically Smart AI™ extracted insights from clinical notes that we couldn’t get anywhere else. This data was instrumental in our successful FDA orphan drug designation.”

VP, Commercial Insights

Leading Biotech Company

Accelerate Your Drug Development and Commercialization

Talk to our team about your specific rare disease or oncology data needs.